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- Health secretary Kennedy launches program to accelerate autism diagnosisU.S. health secretary Robert F. Kennedy Jr. announced a new initiative aimed at speeding up autism assessments during a keynote at a Children’s Health Defense conference. He said the existing diag…
- STAT+: FDA approves a new gene therapy for Sanfilippo syndrome, an ultra-rare diseaseThe FDA approved a new gene therapy for Sanfilippo syndrome type A, an ultra-rare disease sometimes known as childhood Alzheimer’s.STAT · 1mo ago↗ source
- Stanford researchers create mice with half human brain tissue using cerebral organoids