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- Astellas revisits gene therapy for XLMTM, offering new hope after earlier setbacksA gene therapy for the rare muscle disorder X‑linked myotubular myopathy (XLMTM) showed mixed results in early trials, with some boys experiencing dramatic recoveries while others died. Astellas P…
- Dr. Silbermann highlights trial design priorities for multiple myeloma, from supportive care to diverse enrollmentDr. Rebecca Silbermann, an associate professor at Oregon Health & Science University, outlined key considerations for designing multiple myeloma clinical trials. She stressed the importance of alig…