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- Gene therapy viral vectors implicated in a child’s tumor, raising safety concernsA recent STAT+ report highlights a case where viral vectors used in gene therapy were found to be associated with a tumor in a young boy. The article notes that investigators have identified a poss…
- Safety-boosting drug may weaken gene therapy efficacy in Dravet syndrome trialEncoded Therapeutics studied a drug meant to improve the safety of gene therapy in children with Dravet syndrome, a severe genetic epilepsy. In the trial of 21 participants, most received steroids…