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- Father spends $70 million on gene therapy trial for daughter with ultra-rare disease, faces FDA hurdlesMatt Wilsey has spent a decade and about $70 million trying to develop a gene therapy for his 15-year-old daughter Grace, who suffers from a fatal ultra-rare disease. His personal quest has turned…
- GSK ends $2.2 billion brain drug partnership with Alector after trial failuresGSK and California‑based biotech Alector have ended their collaboration after both experimental brain drugs failed to meet development milestones. The partnership, announced in July 2021, gave GSK…