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- Congressional panel warns US rare-disease lead is eroding and calls for supportive policiesA Congressional advisory panel has urged the U.S. government to adopt policies that would help rare disease drug development, including a finalized FDA platform designation and the use of novel tri…
- Crystalys Therapeutics raises $130M to launch gout drug in US and EuropeSan Diego‑based Crystalys Therapeutics announced a new $130 million Series B financing round. The capital will be used to advance its gout treatment, which already holds regulatory approval in Japa…