Encoded Therapeutics gene therapy cuts seizures 76% in Dravet syndrome children
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Encoded Therapeutics presented data at the ASGCT26 meeting showing its gene therapy achieved a 76% reduction in seizures among children with Dravet syndrome.
The result was observed in three patients who received the second-highest dose out of four dose levels tested, suggesting a dose-response trend.
These early findings point to a potential new treatment for the severe neurodevelopmental disorder, though larger studies will be needed to confirm safety and efficacy.
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This writeup was produced by pharmadog from original reporting by Endpoints.
Original headline: “#ASGCT26: Encoded's gene therapy reduced seizures in Dravet syndrome”
read at Endpoints ↗86 words · retrieved May 14
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