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  1. pharmadog
  2. ›drugs
  3. ›vatiquinone
drug · small molecule
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vatiquinone

Phase 3updated 3mo ago
by $PTC PTC INC.🔗 ChEMBL
Phase 3
community read0 votes

Small molecule drug with a maximum clinical stage of Phase 3 (across all indications), with 10 investigational indications.

targets

NAD(P)H dehydrogenase [quinone] 1

all catalysts(0)

nothing on the calendar yet

Trials studying vatiquinone

  • phase3A Study to Assess the Efficacy and Safety of Vatiquinone for the Treatment of Participants With Friedreich Ataxiacompletedn=146
  • —Vatiquinone Expanded Access Protocolno longer available
  • phase3A Study to Evaluate Efficacy and Safety of Vatiquinone for Treating Mitochondrial Disease in Participants With Refractory Epilepsyterminatedn=68
  • phase3A Safety Study for Previously Treated Vatiquinone (PTC743) Participants With Inherited Mitochondrial Diseasecompletedn=101
  • phase3A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxiaactive not recruitingn=130
  • phase2A Study of Vatiquinone for the Treatment of Participants With Friedreich Ataxiacompletedn=5

News(0)

no news has mentioned this drug yet

generic
vatiquinone
MOA
Quinone reductase 1 modulator
indication
MELAS Syndrome (Mitochondrial Encephalomyopathy, Lactic Acidosis and Stroke-Like Episodes)
phase
phase_3
Data sources
ClinicalTrials.gov · OpenTargets
last refreshed 40m ago
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