clinical trial · NCT07159139
Vatiquinone Expanded Access Protocol
Medical University of South Carolina·—·no longer available
Mitochondrial DiseaseVatiquinone
brief summary
The purpose of this study is to provide participants who successfully completed the study titled "An Open-label, Safety Study for Previously Treated Vatiquinone (PTC743) Subjects With Inherited Mitochondrial Disease" with liquid Vatiquinone through an intermediate patient population expanded access protocol.
started
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primary completion
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completion
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last updated
Apr 9, 2026
detailed description
This expanded access protocol serves to make Vatiquinone accessible to subjects with inherited mitochondrial disease who previously participated in a Vatiquinone clinical trial at the Medical University of South Carolina (MUSC) who in the opinion of the investigator would benefit from continued access to liquid Vatiquinone.
official title
Expanded Access Protocol for Vatiquinone in Previously Treated Patients With Inherited Mitochondrial Disease
sourced from ClinicalTrials.gov · pharmadog mirrors structured fields, not the full protocol