clinical trial · NCT07455864
Lysosomal Acid Lipase Deficiency in Risk Groups
AstraZeneca·—·recruiting·n = 1,200
Lysosomal Acid Lipase Deficiency
brief summary
A multicenter real-world observational study of the prevalence, diagnostic pathways, and clinical characteristics of lysosomal acid lipase deficiency in pediatric and adolescent risk groups in the Russian Federation (HELIOS)
started
Feb 25, 2026
primary completion
Jun 30, 2028
completion
Jun 30, 2028
last updated
Apr 14, 2026
official title
A Multicenter Real-world Observational Study of the Prevalence, Diagnostic Pathways, and Clinical Characteristics of Lysosomal Acid Lipase Deficiency in Pediatric and Adolescent Risk Groups in the Russian Federation (HELIOS)
sourced from ClinicalTrials.gov · pharmadog mirrors structured fields, not the full protocol