clinical trial · NCT06952686
A Study of SRP-9005 in Limb Girdle Muscular Dystrophy Type 2C/R5 Pediatric and Adult Participants
Muscular Dystrophies, Limb-GirdleSRP-9005Corticosteroid
brief summary
This is a study of a single systemic dose of SRP-9005 in pediatric and adult participants with limb girdle muscular dystrophy type 2C/R5 (LGMD2C/R5). It is comprised of 2 parts (Part A, Part B) that will assess safety and efficacy.
started
Jun 30, 2025
primary completion
Nov 30, 2030
completion
Mar 30, 2032
last updated
Aug 6, 2025
official title
A Seamless Phase 1/3, Multicenter, Single Dose Systemic Gene Transfer Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9005 in Limb Girdle Muscular Dystrophy Type 2C/R5 Subjects (COMPASS)
sourced from ClinicalTrials.gov · pharmadog mirrors structured fields, not the full protocol