AFFINITY BEYOND: Anti-AAV8 Antibody Assessment Study of Males With DMD
brief summary
This is an observational screening study to evaluate the prevalence of anti-adeno-associated serotype 8 (AAV8) antibodies in participants with Duchenne muscular dystrophy (DMD).
detailed description
This is an observational screening study to evaluate the prevalence of anti-adeno-associated serotype 8 (AAV8) antibodies in participants with Duchenne muscular dystrophy (DMD). Information collected in this study may be used to identify potential participants for DMD investigational gene therapy clinical trials.
This study consists of:
* A phone/video interview or at an in-clinic visit to provide e-consent and medical history * A single home health visit or subsequent in-clinic visit to collect blood sample for antibody testing * A phone/video call for communication of AAV8 antibody test results
official title
Anti-AAV8 Antibody Assessment Study of Males With Duchenne Muscular Dystrophy Aged 0 to <25 Years