clinical trial · NCT05618379
Adult Spinal Muscular Atrophy (SMA) China Registry
Biogen·—·active not recruiting·n = 200
Muscular Atrophy, Spinal
brief summary
The primary objective of the study is to describe the natural history and utilization of disease modifying therapy (DMT) among adult Chinese participants with SMA linked to chromosome 5q (5q-SMA).
started
Jan 6, 2023
primary completion
Jun 1, 2028
completion
Jun 1, 2028
last updated
Jul 11, 2025
official title
Adult Patients With Spinal Muscular Atrophy in China: A Nationwide Registry
sourced from ClinicalTrials.gov · pharmadog mirrors structured fields, not the full protocol