clinical trial · NCT05506254
Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy
Alexion Pharmaceuticals, Inc.·—·active not recruiting·n = 4
Methylmalonic AcidemiahLB-001
brief summary
This is a non-interventional long-term follow-up study of patients who have participated in LogicBio studies for the treatment of MMA and received hLB-001
started
Jul 15, 2022
primary completion
Jan 1, 2037
completion
Jan 1, 2037
last updated
Feb 5, 2026
detailed description
Patients will be followed for a period of 15 years which includes the duration of time that the patient was in the treatment study.
official title
A Long-term Follow-up Study of Patients in LogicBio Clinical Trials for Methylmalonic Acidemia Characterized by MMUT Mutations Who Received hLB-001
sourced from ClinicalTrials.gov · pharmadog mirrors structured fields, not the full protocol