clinical trial · NCT05112237
Natural History Study in Pediatric Patients With MYBPC3 Mutation-associated Cardiomyopathy
Cardiomyopathy
brief summary
The objective of this study is to collect information on patients with cardiomyopathy (CM) due to mutations in the MYBPC3 gene, to evaluate their disease course, burden of illness, risk factors for this disease, and the quality of life (QoL). This study will also collect information on treatments, procedures and outcome in infants and children up to 18 yrs who have this mutation.
started
Nov 1, 2021
primary completion
Jun 1, 2028
completion
Jun 1, 2028
last updated
Nov 13, 2024
official title
A Prospective and Retrospective Registry and Biomarker Study to Evaluate the Natural History of Pediatric Patients With Cardiomyopathy Due to MYBPC3 Mutations
sourced from ClinicalTrials.gov · pharmadog mirrors structured fields, not the full protocol