clinical trial · NCT04626674
A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)
Muscular Dystrophy, Duchennedelandistrogene moxeparvovec
brief summary
This is an open-label gene transfer therapy study evaluating the safety of and expression from delandistrogene moxeparvovec in participants with DMD. The maximum participant duration for this study is 156 weeks.
started
Nov 23, 2020
primary completion
Dec 31, 2027
completion
Feb 29, 2028
last updated
Apr 6, 2026
detailed description
Enrollment for Cohorts 1 through 7 has been completed. Cohort 8 is currently enrolling new participants.
official title
An Open-Label, Systemic Gene Delivery Study Using Commercial Process Material to Evaluate the Safety of and Expression From SRP-9001 in Subjects With Duchenne Muscular Dystrophy (ENDEAVOR)
sourced from ClinicalTrials.gov · pharmadog mirrors structured fields, not the full protocol