clinical trial · NCT03775174
Expanded Access to Mepsevii
MPS VIIMucopolysaccharidosis VIISly SyndromeMepsevii
brief summary
Individual patient expanded access requests may be considered for patients who have no other treatment options
started
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primary completion
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completion
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last updated
Apr 7, 2026
detailed description
Expanded access may be available outside of the US in countries prior to approval by the local regulatory agencies. For full details, please visit the links provided below.
sourced from ClinicalTrials.gov · pharmadog mirrors structured fields, not the full protocol