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- FDA approves Zanvastro, first therapy targeting protein buildup in Alexander diseaseThe U.S. Food and Drug Administration has approved Zanvastro (zilganersen) injection for the treatment of Alexander disease in both pediatric and adult patients. Zanvastro is the first FDA-approve…
- Scaling CAR-T: The hidden challenge of thousands of patient-specific manufacturing runsLegend Biotech and Johnson & Johnson’s Carvykti therapy illustrates the personal connection patients have with CAR-T, but also its unique operating model where each commercial dose is linked to an…