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Endpoints·3h ago·1 min read
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UniQure shares tumble as Huntington's gene therapy shows reduced benefit over time

Sep 29, 2026·read at Endpoints ↗Negative readoutNegative

UniQure announced new follow-up data from its experimental gene therapy for Huntington's disease, indicating the treatment's effect may diminish with longer observation.

The additional year of data showed a waning benefit compared with earlier results, prompting concerns among investors and analysts about the therapy's potential.

Following the disclosure, UniQure's stock price fell sharply on Tuesday morning, reflecting market reaction to the less-optimistic efficacy outlook.

source

This writeup was produced by pharmadog from original reporting by Endpoints.

Original headline: “UniQure sinks as Huntington's gene therapy appears to show waning benefit over time”

read at Endpoints ↗
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Gene Therapy (AAV)3Huntington's2

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