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Phase 2
Gene Therapy to Activate Artemis for Severe Combined Immune Deficiency
Severe Combined Immune Deficiency (SCID)
University of California San Francisco
Preclinical
Gene Therapy to Activate CD40LG for Genetic Disorders
no indication
University of California Los Angeles
Preclinical
Gene Therapy to Activate FOXP3 for Immune Dysregulation Polyendocrinopathy X-linked (IPEX) Syndrome
no indication
ImmunoVec Inc
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131
Pain
89
Neurology
1
Phase 2
Gene Therapy to Activate IL-2 Gamma Receptor for SCID-X1
X-Linked SCID
Boston Children's Hospital
Preclinical
Gene Therapy to Activate PCCA for Propionic Acidemia
Propionic Acidemia
National Institutes of Health
Phase 2
Gene Therapy to Activate Retinoschisin for X-Linked Retinoschisis
Retinal Degeneration
National Eye Institute
Preclinical
Gene Therapy to Activate gp91phox for Chronic Granulomatous Disease
Chronic Granulomatous Disease
ImmunoVec Inc
Preclinical
Gene Therapy to Target BCMA and CS1 for Multiple Myeloma
Multiple Myeloma (Kahler Disease)
University of California Los Angeles
Phase 1
Gene Therapy to Target CD22 for Oncology
B-Cell Acute Lymphocytic Leukemia (B-Cell Acute Lymphobla…
National Cancer Institute US
Preclinical
Genetically Engineered Native Bacteria
Familial Adenomatous Polyposis
Endure Biotherapeutics
Marketed
Geodon
Geodon (ziprasidone hydrochloride)
Bipolar Disorder (Manic Depression)
$VTRS
Viatris Inc
Preclinical
Gliflozins
Congestive Heart Failure (Heart Failure)
$RTX
RTX Corp
Preclinical
Glucokinase Regulator
Hyperinsulinemia
Hua Medicine Shanghai Ltd
Preclinical
Glunozumab
Unspecified
Lys Therapeutics SAS
Preclinical
GlyTR1 Bi-specific Protein
Solid Tumor
GlyTR Therapeutics Inc
Preclinical
Glycogen Storage Disease 1B
Glycogen Storage Disease (GSD)
$PRME
Prime Medicine, Inc.
Preclinical
Glycolic acid + D-lactic acid
Amyotrophic Lateral Sclerosis
Neurevo GmbH
Preclinical
Granulocyte Colony-Stimulating-Factor (G-CSF)
Thromboangiitis obliterans (Buerger disease)
Vasogenesis Inc
Preclinical
Granzyme B Associated Peptide
Herpes Simplex Encephalitis
Biojenc LLC
Phase 2
H-002
Non-Small Cell Lung Cancer
RedCloud Bio Inc
Phase 1
H-100
H100
Peyronies Disease
$PTPI
Petros Pharmaceuticals, Inc.
Phase 2
H-1337
Open-Angle Glaucoma
D. Western Therapeutics Institute Inc
Phase 1
H-3B6545
Human Epidermal Growth Factor Receptor 2 Negative Breast…
Eisai Co Ltd
HAILEY 24 FE
HAILEY 24 FE (NORETHINDRONE ACETATE AND ETHINYL ESTRADIOL, AND FERROUS FUMARATE)
no indication
GLENMARK PHARMS LTD
HALCINONIDE TOPICAL SOLUTION
HALCINONIDE TOPICAL SOLUTION (HALCINONIDE TOPICAL)
no indication
ENCUBE
Phase 2
HB-adMSC Allogeneic
Crohn's Disease (Regional Enteritis)
Hope Biosciences LLC
Phase 3
HB-adMSCs
Spinal Cord Injury
Hope Biosciences LLC
Phase 2
HBI-3000
Atrial Fibrillation
HUYA Bioscience International LLC
Phase 1
HBM-1020
Metastatic Colorectal Cancer
Harbour BioMed (Guangzhou) Co Ltd
Preclinical
HBO-001
no indication
HysensBio Corp