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Phase 3
delpacibart braxlosiran
delpacibart braxlosiran [INN]
Facioscapulohumeral Muscular Dystrophy (FSHD)
Avidity Biosciences Inc
Phase 3
delpacibart etedesiran
delpacibart etedesiran [INN]
Myotonic Dystrophy
Avidity Biosciences Inc
Phase 3
deramciclane + dextromethorphan
(deramciclane [INN] + dextromethorphan [INN])
Psychiatric Disorders
Exciva GmbH
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131
Pain
89
Neurology
1
Phase 3
dersimelagon phosphate
dersimelagon phosphate
Erythropoietic Protoporphyria
Tanabe Pharma Corp
Phase 3
deupsilocin besylate
deupsilocin besylate
Major Depressive Disorder
HELUS Pharma
Phase 3
dexamethasone sodium phosphate
SEMDEXA (dexamethasone sodium phosphate)
Ataxia-Telangiectasia (Louis-Bar Syndrome)
$QNCX
Quince Therapeutics, Inc.
Phase 3
diiodothyropropionic acid
Allan-Herndon-Dudley Syndrome (Monocarboxylate Transporte…
Prizm LLC
Phase 3
direclidine citrate
direclidine citrate
Schizophrenia
$NBIX
NEUROCRINE BIOSCIENCES INC
Phase 3
divarasib
divarasib
Non-Small Cell Lung Cancer
Genentech Inc
Phase 3
dotinurad
dotinurad [INN]
Gouty Arthritis (Gout)
Crystalys Therapeutics Inc
Phase 3
dulpatatug
dulpatatug [INN]
Adenocarcinoma Of The Gastroesophageal Junction
Shanghai Henlius Biotech Inc
Phase 3
duvakitug
duvakitug
Crohn's Disease (Regional Enteritis)
$TEVA
TEVA PHARMACEUTICAL INDUSTRIES LTD
Phase 3
ebselen
ebselen [INN]
Meniere Disease
$SOGP
Sound Group Inc.
Phase 3
ecopipam hydrochloride
ecopipam hydrochloride
Tourette Syndrome
Emalex Biosciences Inc
Phase 3
eflornithine
eflornithine [INN]
Anaplastic Astrocytoma
Orbus Therapeutics Inc
Phase 3
efmirenpase alfa
efmirenpase alfa [INN]
Arterial Calcification
$BMRN
BIOMARIN PHARMACEUTICAL INC
Phase 3
efruxifermin
efruxifermin
Metabolic Dysfunction-Associated Steatohepatitis (MASH or…
Akero Therapeutics Inc
Phase 3
efsudenermin alfa
efsudenermin alfa
X-Linked Hypohidrotic Ectodermal Dysplasia (XLHED)
EspeRare Foundation
Phase 3
eftilagimod alfa
eftilagimod alfa [INN]
Human Epidermal Growth Factor Receptor 2 Negative Breast…
$IMMP
IMMUTEP Ltd
Phase 3
efzimfotase alfa
efzimfotase alfa
Hypophosphatasia
Alexion Pharmaceuticals Inc
Phase 3
elebsiran
elebsiran
Hepatitis D
$VIR
Vir Biotechnology, Inc.
Phase 3
elebsiran + tobevibart
elebsiran + tobevibart
Hepatitis D
$VIR
Vir Biotechnology, Inc.
Phase 3
elegrobart
elegrobart
Graves' Ophthalmopathy
Viridian Therapeutics Inc
Phase 3
elenestinib
elenestinib
Systemic Mastocytosis
Blueprint Medicines Corp
Phase 3
elfucose
elfucose
Inherited Metabolic Disorders
AUG Therapeutics LLC
Phase 3
elritercept
elritercept
Anemia
$TAK
TAKEDA PHARMACEUTICAL CO LTD
Phase 3
elsunersen
elsunersen [INN]
Epileptic Encephalopathy
$PRAX
Praxis Precision Medicines, Inc.
Phase 3
emactuzumab
emactuzumab
Tenosynovial Giant Cell Tumor
SynOx Therapeutics Ltd
Phase 3
emestedastat
Xanamem (emestedastat)
Alzheimer's Disease
Actinogen Medical Ltd
Phase 3
emixustat hydrochloride
emixustat hydrochloride
Juvenile Macular Degeneration (Stargardt Disease)
Kubota Vision Inc