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Phase 2
voretigene neparvovec
Luxturna (voretigene neparvovec-rzyl)
Choroideremia
F. Hoffmann-La Roche Ltd
Phase 2
vosilasarm
vosilasarm
Human Epidermal Growth Factor Receptor 2 Negative Breast…
Ellipses Pharma Ltd
Phase 2
vusolimogene oderparepvec
vusolimogene oderparepvec
Basal Cell Carcinoma (Basal Cell Epithelioma)
$REPL
Replimune Group, Inc.
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131
Pain
89
Neurology
1
Phase 2
xelafaslatide
xelafaslatide
Retinal Pigment Epithelial (RPE) Detachment
ONL Therapeutics Inc
Phase 2
zabilugene almadenorepvec
zabilugene almadenorepvec
Pancreatic Ductal Adenocarcinoma
$TOVX
Theriva Biologics, Inc.
Phase 2
zagociguat
zagociguat
MELAS Syndrome (Mitochondrial Encephalomyopathy, Lactic A…
Tisento Therapeutics Inc
Phase 2
zalifrelimab
zalifrelimab
Cervical Cancer
$AGEN
AGENUS INC
Phase 2
zaltenibart
zaltenibart
Paroxysmal Nocturnal Hemoglobinuria
Novo Nordisk AS
Phase 2
zampilimab
zampilimab [INN]
Idiopathic Pulmonary Fibrosis
Chiesi Farmaceutici SpA
Phase 2
zegocractin
zegocractin
Pancreatitis
$CALC
CalciMedica, Inc.
Phase 2
zeleciment basivarsen
zeleciment basivarsen
Myotonic Dystrophy
$DYN
Dyne Therapeutics, Inc.
Phase 2
zeleciment rostudirsen
zeleciment rostudirsen
Duchenne Muscular Dystrophy
$DYN
Dyne Therapeutics, Inc.
Phase 2
zelenirstat
zelenirstat [INN]
Refractory Acute Myeloid Leukemia
Pacylex Pharmaceuticals Inc
Phase 2
zelicapavir
zelicapavir
Respiratory Syncytial Virus (RSV) Infections
$ENTA
ENANTA PHARMACEUTICALS INC
Phase 2
zelquistinel
zelquistinel [INN]
Major Depressive Disorder
Syndeio Biosciences Inc
Phase 2
zemocimig
zemocimig [INN]
Hemophilia A (Factor VIII Deficiency)
F. Hoffmann-La Roche Ltd
Phase 2
zenuzolac
zenuzolac [INN]
Coronavirus Disease 2019 (COVID-19) Pneumonia
GeneOne Life Science Inc
Phase 2
zerlasiran sodium
zerlasiran sodium
Atherosclerosis
$SLN
Silence Therapeutics plc
Phase 2
zervimesine
Elayta (zervimesine)
Alzheimer's Disease
$CGTX
COGNITION THERAPEUTICS INC
Phase 2
zetomipzomib maleate
zetomipzomib maleate
Autoimmune Hepatitis
$KZR
Kezar Life Sciences, Inc.
Phase 2
zevotrelvir
zevotrelvir
Coronavirus Disease 2019 (COVID-19)
$ENTA
ENANTA PHARMACEUTICALS INC
Phase 2
zileuton
zileuton
Atopic Dermatitis (Atopic Eczema)
Qurient Co Ltd
Phase 2
zilovertamab vedotin
zilovertamab vedotin [INN]
Mantle Cell Lymphoma
$MRK
Merck & Co., Inc.
Phase 2
zilurgisertib fumarate
zilurgisertib fumarate
Fibrodysplasia Ossificans Progressiva (Myositis Ossifican…
$INCY
INCYTE CORP
Phase 2
zimberelimab
zimberelimab
Adenocarcinoma Of The Gastroesophageal Junction
$RCUS
Arcus Biosciences, Inc.
Phase 2
zocaglusagene nuzaparvovec
zocaglusagene nuzaparvovec
Pompe Disease
Astellas Pharma Inc
Phase 2
zodasiran sodium
zodasiran sodium
Familial Hypercholesterolemia (Type II Hyperlipoproteinemia)
$ARWR
ARROWHEAD PHARMACEUTICALS, INC.
Phase 2
zolbetuximab
Vyloy (zolbetuximab-clzb)
Metastatic Adenocarcinoma of The Pancreas
Astellas Pharma Inc
Phase 2
zolucatetide
zolucatetide [INN]
Craniopharyngioma
Parabilis Medicines
Phase 2
zotiraciclib citrate
zotiraciclib citrate
Glioblastoma Multiforme (GBM)
Beijing zhikangbo Medical Oncology Research Co Ltd