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Preclinical
Gene Therapy for Bone Fracture
Bone Fracture
Cedars-Sinai Medical Center
Preclinical
Gene Therapy for Branched-Chain 2-Ketoacid Dehydrogenase Deficiency
Maple Syrup Urine Disease
Clinic for Special Children
Preclinical
Gene Therapy for Limb-Girdle Muscular Dystrophy Type 2C/R5
Limb-Girdle Muscular Dystrophy
Evolyra Therapeutics
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131
Pain
89
Neurology
1
Preclinical
Gene Therapy to Activate CD40LG for Genetic Disorders
no indication
University of California Los Angeles
Preclinical
Gene Therapy to Activate FOXP3 for Immune Dysregulation Polyendocrinopathy X-linked (IPEX) Syndrome
no indication
ImmunoVec Inc
Preclinical
Gene Therapy to Activate PCCA for Propionic Acidemia
Propionic Acidemia
National Institutes of Health
Preclinical
Gene Therapy to Activate gp91phox for Chronic Granulomatous Disease
Chronic Granulomatous Disease
ImmunoVec Inc
Preclinical
Gene Therapy to Target BCMA and CS1 for Multiple Myeloma
Multiple Myeloma (Kahler Disease)
University of California Los Angeles
Preclinical
Genetically Engineered Native Bacteria
Familial Adenomatous Polyposis
Endure Biotherapeutics
Preclinical
Gliflozins
Congestive Heart Failure (Heart Failure)
$RTX
RTX Corp
Preclinical
Glucokinase Regulator
Hyperinsulinemia
Hua Medicine Shanghai Ltd
Preclinical
Glunozumab
Unspecified
Lys Therapeutics SAS
Preclinical
GlyTR1 Bi-specific Protein
Solid Tumor
GlyTR Therapeutics Inc
Preclinical
Glycogen Storage Disease 1B
Glycogen Storage Disease (GSD)
$PRME
Prime Medicine, Inc.
Preclinical
Glycolic acid + D-lactic acid
Amyotrophic Lateral Sclerosis
Neurevo GmbH
Preclinical
Granulocyte Colony-Stimulating-Factor (G-CSF)
Thromboangiitis obliterans (Buerger disease)
Vasogenesis Inc
Preclinical
Granzyme B Associated Peptide
Herpes Simplex Encephalitis
Biojenc LLC
Preclinical
HBO-001
no indication
HysensBio Corp
Preclinical
HFG-1
Diabetes
HighField Biopharmaceuticals, Inc.
Preclinical
HIV Vaccine
Human Immunodeficiency Virus (HIV) Infections (AIDS)
DelSiTech Ltd
Preclinical
HL-001
Idiopathic Pulmonary Fibrosis
UBE Corp
Preclinical
HLH Therapy
Hemophagocytic Lymphohistiocytosis
GenexGen Inc
Preclinical
HNC-1798
Parkinson's Disease
Guangzhou Henovcom Bioscience Co Ltd
Preclinical
HNC-280
Hepatitis B
Guangzhou Henovcom Bioscience Co Ltd
Preclinical
HND-034
Lung Cancer
Handa Pharmaceuticals LLC
Preclinical
HND-039
Kidney Cancer (Renal Cell Cancer)
Handa Pharmaceuticals LLC
Preclinical
HND-042
Unspecified Cancer
Handa Pharmaceuticals LLC
Preclinical
HP-520
no indication
Hinova Pharmaceuticals Inc
Preclinical
HT-ALZ
Alzheimer's Disease
$HOTH
Hoth Therapeutics, Inc.
Preclinical
HT-KIT
Anaphylaxis
$HOTH
Hoth Therapeutics, Inc.