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Preclinical
GIVI-MPC
Duchenne Muscular Dystrophy
IPS Heart Inc
Preclinical
GLR-2007
Malignant Glioma
Gan & Lee Pharmaceuticals Co Ltd
Preclinical
GM-0111
Oral Mucositis
GlycoMira Therapeutics Inc
Preclinical
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131
Pain
89
Neurology
1
GNT-0008
Limb-Girdle Muscular Dystrophy
Atamyo Therapeutics SAS
Preclinical
GNTbm-TKI
Neuroendocrine Tumors
Great Novel Therapeutics Biotech & Medicals Corp
Preclinical
GP-119
Alzheimer's Disease
GliaPharm SA
Preclinical
GPX-002
Type 1 Diabetes (Juvenile Diabetes)
$GNPX
Genprex, Inc.
Preclinical
GRI-0803
Systemic Lupus Erythematosus
$GRI
GRI Bio, Inc.
Preclinical
GTC-3295
Alzheimer's Disease
Gismo Therapeutics Inc
Preclinical
GW-01
Unspecified Cancer
Groovy Medicine Inc
Preclinical
GXC-301
Lafora Disease (Unverricht Disease)
Genixcure Inc
Preclinical
GXV-002
Pulmonary Arterial Hypertension
GEXVal Inc
Preclinical
Gene Therapies to Activate NAGLU for Mucopolysaccharidosis Type IIIB
Mucopolysaccharidosis III (MPS III) (Sanfilippo Syndrome )
Neurogt Inc
Preclinical
Gene Therapy Product
Chemotherapy Induced Peripheral Neuropathy
Navega Therapeutics Inc
Preclinical
Gene Therapy for Alpha-Mannosidosis
Alpha-Mannosidosis
Eunice Kennedy Shriver National Institute of Child Health and Human Development
Preclinical
Gene Therapy for Arginase 1 Deficiency
Hyperargininemia (Arginase I Deficiency)
UCLA Health System
Preclinical
Gene Therapy for Bone Fracture
Bone Fracture
Cedars-Sinai Medical Center
Preclinical
Gene Therapy for Branched-Chain 2-Ketoacid Dehydrogenase Deficiency
Maple Syrup Urine Disease
Clinic for Special Children
Preclinical
Gene Therapy for Limb-Girdle Muscular Dystrophy Type 2C/R5
Limb-Girdle Muscular Dystrophy
Evolyra Therapeutics
Preclinical
Gene Therapy to Activate CD40LG for Genetic Disorders
no indication
University of California Los Angeles
Preclinical
Gene Therapy to Activate FOXP3 for Immune Dysregulation Polyendocrinopathy X-linked (IPEX) Syndrome
no indication
ImmunoVec Inc
Preclinical
Gene Therapy to Activate PCCA for Propionic Acidemia
Propionic Acidemia
National Institutes of Health
Preclinical
Gene Therapy to Activate gp91phox for Chronic Granulomatous Disease
Chronic Granulomatous Disease
ImmunoVec Inc
Preclinical
Gene Therapy to Target BCMA and CS1 for Multiple Myeloma
Multiple Myeloma (Kahler Disease)
University of California Los Angeles
Preclinical
Genetically Engineered Native Bacteria
Familial Adenomatous Polyposis
Endure Biotherapeutics
Preclinical
Gliflozins
Congestive Heart Failure (Heart Failure)
$RTX
RTX Corp
Preclinical
Glucokinase Regulator
Hyperinsulinemia
Hua Medicine Shanghai Ltd
Preclinical
Glunozumab
Unspecified
Lys Therapeutics SAS
Preclinical
GlyTR1 Bi-specific Protein
Solid Tumor
GlyTR Therapeutics Inc
Preclinical
Glycogen Storage Disease 1B
Glycogen Storage Disease (GSD)
$PRME
Prime Medicine, Inc.