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Phase 3
pitolisant GR
pitolisant [INN]
Narcolepsy
$HRMY
Harmony Biosciences Holdings, Inc.
Phase 3
pivodisgene parvec
pivodisgene parvec [INN]
Duchenne Muscular Dystrophy
$RGNX
REGENXBIO Inc.
Phase 3
plasminogen concentrate
Conjunctivitis
Kedrion SpA
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131
Pain
89
Neurology
1
Phase 3
plastoquinone decyl triphenylphosphonium bromide
Visomitin
Keratoconjunctivitis Sicca (Dry Eye)
Mitotech SA
Phase 3
plinabulin
plinabulin
Febrile Neutropenia
$BYSI
BeyondSpring Inc.
Phase 3
pneumococcal conjugate (21-valent) vaccine
Pneumonia
SK Bioscience Ltd
Phase 3
polihexanide
Akantior (polihexanide)
Parasitic (Acanthamoeba) Corneal Ulcers
SIFI SpA
Phase 3
potravitug
potravitug
Polyomavirus Infections
Memo Therapeutics AG
Phase 3
povetacicept
povetacicept
Membranous Glomerulonephritis
$VERX
Vertex, Inc.
Phase 3
pozdeutinurad
pozdeutinurad
Gouty Arthritis (Gout)
Arthrosi Therapeutics Inc
Phase 3
pozelimab
Veopoz (pozelimab-bbfg)
Myasthenia Gravis
$REGN
REGENERON PHARMACEUTICALS, INC.
Phase 3
prasinezumab
prasinezumab
Parkinson's Disease
Prothena Corp Plc
Phase 3
pridopidine hydrochloride
Huntexil (pridopidine hydrochloride)
Amyotrophic Lateral Sclerosis
Prilenia Therapeutics BV
Phase 3
propagermanium
QYTOVRA (propagermanium [INN])
Focal Segmental Glomerulosclerosis (FSGS)
$FOLD
AMICUS THERAPEUTICS, INC.
Phase 3
psilocybin
psilocybin
Treatment Resistant Depression
$CMPS
COMPASS Pathways plc
Phase 3
pumitamig
pumitamig [INN]
Non-Small Cell Lung Cancer
$BNTX
BioNTech SE
Phase 3
quabodepistat
quabodepistat
Pulmonary Tuberculosis
Otsuka Pharmaceutical Co Ltd
Phase 3
quemliclustat
quemliclustat
Pancreatic Ductal Adenocarcinoma
$RCUS
Arcus Biosciences, Inc.
Phase 3
radiprodil
radiprodil
Unspecified Neurologic Disorders
GRIN Therapeutics Inc
Phase 3
rafutrombopag
rafutrombopag [INN]
Thrombocytopenia
Jiangsu Hengrui Pharmaceuticals Co Ltd
Phase 3
ralinepag XR
ralinepag
Pulmonary Arterial Hypertension
$UTHR
UNITED THERAPEUTICS Corp
Phase 3
ramucirumab
Cyramza (ramucirumab)
Adenocarcinoma Of The Gastroesophageal Junction
Eli Lilly and Co
Phase 3
rebonuputemcel
rebonuputemcel
Degenerative Disc Disease
DiscGenics Inc
Phase 3
reboxetine
reboxetine [INN]
Type 1 Narcolepsy (Narcolepsy with Cataplexy)
$AXSM
Axsome Therapeutics, Inc.
Phase 3
remestemcel-L
Prochymal (remestemcel-L)
Crohn's Disease (Regional Enteritis)
$MESO
MESOBLAST LTD
Phase 3
remlifanserin
remlifanserin
Alzheimer's Disease
$ACAD
ACADIA PHARMACEUTICALS INC
Phase 3
repinatrabit
repinatrabit
Phenylketonuria (PKU)
Jnana Therapeutics Inc
Phase 3
resecabtagene autoleucel
resecabtagene autoleucel [INN]
Juvenile Dermatomyositis
$CABA
Cabaletta Bio, Inc.
Phase 3
resiniferatoxin
resiniferatoxin [INN]
Osteoarthritis Pain
Grunenthal GmbH
Phase 3
retogatein
Diamyd (retogatein)
Type 1 Diabetes (Juvenile Diabetes)
Diamyd Medical AB