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Preclinical
3Z-20002
Attention Deficit Hyperactivity Disorder (ADHD)
3Z ehf
Preclinical
3Z-20004
Attention Deficit Hyperactivity Disorder (ADHD)
3Z ehf
Preclinical
4-hydroxybenzoic acid
Inherited Mitochondrial Disorders
New York University
Preclinical
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131
Pain
89
Neurology
1
4P FSH
Female Infertility
$NTRB
NutriBand Inc.
Preclinical
4WJ-CPTH-FUDR-FTD
Liver Cancer
RNA NanoBiotics Inc
Preclinical
4WJ-FUDR-GEM
Triple-Negative Breast Cancer (TNBC)
RNA NanoBiotics Inc
Preclinical
6SP-001
Oral Mucositis
6S Pharma LLC
Preclinical
6SP-002
Diabetic Foot Ulcers
6S Pharma LLC
Preclinical
6SP-003
Burns
6S Pharma LLC
Preclinical
6SP-2405
Uterine Leiomyoma (Uterine Fibroids)
6S Pharma LLC
Preclinical
6SP-2406 ER
Sicca Syndrome (Sjogren)
6S Pharma LLC
Preclinical
6SP-2407
Macular Degeneration
6S Pharma LLC
Preclinical
6SP-2408
Leptomeningeal Disease (Neoplastic Meningitis, Leptomenin…
6S Pharma LLC
Preclinical
6SP-2409
Gastric Ulcers
6S Pharma LLC
Preclinical
A-83B4C63
Colorectal Cancer
Onco Innovations Ltd
Preclinical
AAV-ATP7A Gene Therapy
Menkes Disease (Kinky Hair Disease)
Cyprium Therapeutics Inc
Preclinical
AAV-RDH12
no indication
$MGTX
MeiraGTx Holdings plc
Preclinical
AAV9 Gene Replacement Therapy
Mucopolysaccharidosis I (MPS I) (Hurler Syndrome )
Neurogt Inc
Preclinical
AAVCOVID
Coronavirus Disease 2019 (COVID-19)
Massachusetts General Hospital
Preclinical
AB-2010
Idiopathic Pulmonary Fibrosis
Alveolus Bio Inc
Preclinical
ABG-023
Hyperinsulinemia
AmideBio LLC
Preclinical
ABI-171
Idiopathic Pulmonary Fibrosis
Avanti Biosciences Inc
Preclinical
ABN-501
Solid Tumor
Abion Inc
Preclinical
ABO-503
Retinal Degeneration
$ABEO
ABEONA THERAPEUTICS INC.
Preclinical
ABO-504
Juvenile Macular Degeneration (Stargardt Disease)
$ABEO
ABEONA THERAPEUTICS INC.
Preclinical
ABO-505
Optic Neuropathy
$ABEO
ABEONA THERAPEUTICS INC.
Preclinical
ABX-919
Atopic Dermatitis (Atopic Eczema)
Abrax Japan
Preclinical
AC-1
Traumatic Brain Injury
AivoCode LLP
Preclinical
ACAR-198
Autoimmune Disorders
AbelZeta Inc
Preclinical
ACM-002
Amyotrophic Lateral Sclerosis
Actimed Therapeutics Ltd