drug · gene
voretigene neparvovec
Phase 2updated 3mo agoby F. Hoffmann-La Roche Ltd🔗 ChEMBL
Phase 2community read0 votes
Gene drug with a maximum clinical stage of Approval (across all indications), with 3 approved and 1 investigational indication.
targets
Retinoid isomerohydrolase
all catalysts(0)
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Trials studying voretigene neparvovec
- —A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US
- phase2Phase 1 Follow-on Study of AAV2-hRPE65v2 Vector in Subjects With Leber Congenital Amaurosis (LCA) 2
- phase3Study of Efficacy and Safety of Voretigene Neparvovec in Japanese Patients With Biallelic RPE65 Mutation-associated Retinal Dystrophy
- phase3Safety and Efficacy Study in Subjects With Leber Congenital Amaurosis
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