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  1. pharmadog
  2. ›drugs
  3. ›Emcitate
drug · small molecule
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tiratricol ODT

pre_registrationupdated 5mo ago
by Egetis Therapeutics AB🔗 ChEMBL
community read0 votes

Small molecule drug with a maximum clinical stage of Approval (across all indications), with an approval for thyrotoxicosis and 3 investigational indications.

targets

Thyroid hormone receptor

all catalysts(0)

nothing on the calendar yet

Trials studying tiratricol ODT

  • —Expanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiencyavailable
  • phase3Withdrawal of Tiratricol Treatment in Males With Monocarboxylate Transporter 8 Deficiency (MCT8 Deficiency)completedn=20
  • phase2Triac Trial II in MCT8 Deficiency Patientsactive not recruitingn=22

News(3)

  • Egetis Therapeutics' Emcitate cleared by FDA for rare X-linked genetic disease
    Egetis Therapeutics has secured US approval of its drug for a rare disease that shortens life expectancy to 35 years. The FDA on Monday backed tiratricol for certain patients with monocarboxylate ...
    endpoints · 6d ago
  • Recon: FDA approves Egetis’ Emcitate for rare genetic disease; Novo buys rights to Chinese weight-loss pill in $2.6B deal
    Welcome to Regulatory Reconnaissance, your regulatory news and intelligence briefing.
    raps · 6d ago
  • FDA Approves First Treatment for MCT8 Deficiency
    The U.S. Food and Drug Administration today approved Emcitate (tiratricol) tablets for oral suspension to treat peripheral thyrotoxicosis (excess thyroid hormone levels in the blood that causes sym…
    fda_press · 6d ago
brand
Emcitate
generic
tiratricol
MOA
Thyroid hormone receptor agonist
indication
Allan-Herndon-Dudley Syndrome (Monocarboxylate Transporter-8 Deficiency)
phase
pre_registration
Data sources
ClinicalTrials.gov · OpenTargets
last refreshed 3h ago
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