drug · gene
pariglasgene brecaparvovec
pre_registrationupdated 3mo agoby $RARE Ultragenyx Pharmaceutical Inc.🔗 ChEMBL
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Gene drug with a maximum clinical stage of Phase 1 (across all indications), with 4 investigational indications.
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nothing on the calendar yet
News(2)
- FDA Approves First Therapy for Patients aged 8 years and older with Glycogen Storage Disease Type IaThe U.S. Food and Drug Administration today issued an accelerated approval for Genglycos (pariglasgene brecaparvovec-opnr) as the first-ever treatment for adults and children 8 years of age and old…fda_press · 3h ago
- Biotechs bring big launches and pharma rivalries into Q2 earnings periodWith the second quarter earnings period underway, BioSpace examines five biotechs with meaningful catalysts that analysts and investors are watching.biospace · 21d ago
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