drug · gene
pariglasgene brecaparvovec
pre_registrationupdated 5mo agoby $RARE Ultragenyx Pharmaceutical Inc.🔗 ChEMBL
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Gene drug with a maximum clinical stage of Phase 1 (across all indications), with 4 investigational indications.
all catalysts(0)
nothing on the calendar yet
News(3)
- Ultragenyx fails phase 3 Angelman test, plots ‘significant expense reductions’Ultragenyx had been flying high after its recent FDA approval for Genglycos—but the company has been brought back down to earth with a damaging phase 3 flop.fiercebiotech · 1mo ago
- FDA Approves First Therapy for Patients aged 8 years and older with Glycogen Storage Disease Type IaThe U.S. Food and Drug Administration today issued an accelerated approval for Genglycos (pariglasgene brecaparvovec-opnr) as the first-ever treatment for adults and children 8 years of age and old…fda_press · 1mo ago
- Biotechs bring big launches and pharma rivalries into Q2 earnings periodWith the second quarter earnings period underway, BioSpace examines five biotechs with meaningful catalysts that analysts and investors are watching.biospace · 2mo ago
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