Genetix Biotherapeutics Inc

Active trials

• —A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcelrecruitingn=120
• —Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapyactive not recruitingn=66
• —Long-term Follow-up of Subjects with Sickle Cell Disease Treated with Ex Vivo Gene Therapyenrolling by invitationn=85
• phase2A Study Evaluating the Safety and Efficacy of Lovo-cel in Severe Sickle Cell Diseasecompletedn=54
• —Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Productactive not recruitingn=64
• —A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcelrecruitingn=150
• phase3A Study Evaluating Gene Therapy With BB305 Lentiviral Vector in Sickle Cell Diseaseactive not recruitingn=35
• phase3A Clinical Study to Assess the Efficacy and Safety of Gene Therapy for the Treatment of Cerebral Adrenoleukodystrophy (CALD)completedn=35